GENE-THERAPY FOR GENETIC-DISEASES

被引:39
作者
KOHN, DB
ANDERSON, WF
BLAESE, RM
机构
[1] NCI,METAB BRANCH,BETHESDA,MD
[2] NHLBI,MOLEC HEMATOL LAB,BETHESDA,MD
关键词
D O I
10.3109/07357908909038283
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
引用
收藏
页码:179 / 192
页数:14
相关论文
共 48 条
[1]   STRUCTURE OF ADENOSINE-DEAMINASE MESSENGER-RNAS FROM NORMAL AND ADENOSINE DEAMINASE-DEFICIENT HUMAN CELL-LINES [J].
ADRIAN, GS ;
WIGINTON, DA ;
HUTTON, JJ .
MOLECULAR AND CELLULAR BIOLOGY, 1984, 4 (09) :1712-1717
[2]   PROSPECTS FOR HUMAN-GENE THERAPY [J].
ANDERSON, WF .
SCIENCE, 1984, 226 (4673) :401-409
[3]   CIRCULATING PLURIPOTENT HEMATOPOIETIC PROGENITOR CELLS IN NEONATES [J].
CHRISTENSEN, RD .
JOURNAL OF PEDIATRICS, 1987, 110 (04) :622-625
[4]  
CORNETTA K, 1988, J CELLULAR BIOCH S, V12, P171
[5]   LINEAGE-SPECIFIC EXPRESSION OF A HUMAN BETA-GLOBIN GENE IN MURINE BONE-MARROW TRANSPLANT RECIPIENTS RECONSTITUTED WITH RETROVIRUS-TRANSDUCED STEM-CELLS [J].
DZIERZAK, EA ;
PAPAYANNOPOULOU, T ;
MULLIGAN, RC .
NATURE, 1988, 331 (6151) :35-41
[6]  
EGLITIS MA, 1988, BLOOD, V71, P717
[7]   GENE-EXPRESSION IN MICE AFTER HIGH-EFFICIENCY RETROVIRAL-MEDIATED GENE-TRANSFER [J].
EGLITIS, MA ;
KANTOFF, P ;
GILBOA, E ;
ANDERSON, WF .
SCIENCE, 1985, 230 (4732) :1395-1398
[8]  
FISCHER A, 1986, LANCET, V2, P1080
[9]  
GIBLETT ER, 1972, LANCET, V2, P1067
[10]   THE ROLE OF ANTISENSE RNA IN GENE-REGULATION [J].
GREEN, PJ ;
PINES, O ;
INOUYE, M .
ANNUAL REVIEW OF BIOCHEMISTRY, 1986, 55 :569-597