HUMAN BETA-GLUCURONIDASE .2. FATE OF INFUSED HUMAN PLACENTAL BETA-GLUCURONIDASE IN RAT

被引:52
作者
ACHORD, D
BROT, F
GONZALEZNORIEGA, A
SLY, W
STAHL, P
机构
[1] ST LOUIS CHILDRENS HOSP, DIV MED GENET, ST LOUIS, MO 63110 USA
[2] WASHINGTON UNIV, SCH MED, EDWARD MALLINCKRODT DEPT PEDIAT, ST LOUIS, MO 63110 USA
[3] WASHINGTON UNIV, SCH MED, DEPT PHYSIOL & BIOPHYS, ST LOUIS, MO 63110 USA
关键词
D O I
10.1203/00006450-197707000-00008
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
引用
收藏
页码:816 / 822
页数:7
相关论文
共 30 条
[1]  
ACHORD DT, 1975, AM J HUM GENET, V27, pA10
[2]  
BRADY RO, 1975, FED PROC, V34, P1310
[3]   REPLACEMENT THERAPY FOR INHERITED ENZYME DEFICIENCY - USE OF PURIFIED GLUCOCEREBROSIDASE IN GAUCHERS-DISEASE [J].
BRADY, RO ;
PENTCHEV, PG ;
GAL, AE ;
HIBBERT, SR ;
DEKABAN, AS .
NEW ENGLAND JOURNAL OF MEDICINE, 1974, 291 (19) :989-993
[4]   REPLACEMENT THERAPY FOR INHERITED ENZYME DEFICIENCY - USE OF PURIFIED CERAMIDETRIHEXOSIDASE IN FABRYS-DISEASE [J].
BRADY, RO ;
TALLMAN, JF ;
JOHNSON, WG ;
GAL, AE ;
LEAHY, WR ;
QUIRK, JM ;
DEKABAN, AS .
NEW ENGLAND JOURNAL OF MEDICINE, 1973, 289 (01) :9-14
[5]   IN-VITRO CORRECTION OF DEFICIENT HUMAN FIBROBLASTS BY BETA-GLUCURONIDASE FROM DIFFERENT HUMAN SOURCES [J].
BROT, FE ;
GLASER, JH ;
ROOZEN, KJ ;
SLY, WS .
BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 1974, 57 (01) :1-8
[6]  
de Barsy T, 1973, Birth Defects Orig Artic Ser, V9, P184
[7]   TOWARD ENZYME THERAPY FOR LYSOSOMAL STORAGE DISEASES [J].
DESNICK, RJ ;
THORPE, SR ;
FIDDLER, MB .
PHYSIOLOGICAL REVIEWS, 1976, 56 (01) :57-99
[8]   TISSUE FRACTIONATION STUDIES .6. INTRACELLULAR DISTRIBUTION PATTERNS OF ENZYMES IN RAT-LIVER TISSUE [J].
DUVE, CD ;
PRESSMAN, BC ;
GIANETTO, R ;
WATTIAUX, R ;
APPELMANS, F .
BIOCHEMICAL JOURNAL, 1955, 60 (1-4) :604-617
[9]   HUMAN BETA-GLUCURONIDASE .1. RECOGNITION AND UPTAKE BY ANIMAL FIBROBLASTS SUGGESTS ANIMAL-MODELS FOR ENZYME REPLACEMENT STUDIES [J].
FRANKEL, HA ;
GLASER, JH ;
SLY, WS .
PEDIATRIC RESEARCH, 1977, 11 (07) :811-816
[10]  
GLASER JH, 1973, J LAB CLIN MED, V82, P969